Final ID:
Ruberg Frederick, Blaner William, Deluca Albert, Johnson Lynne, Kinkhabwala Mona, Leb Jay, Mintz Akiva, Lavalley Michael, Einstein Andrew, Cohn Elizabeth, Kelly Jeffery, Teruya Sergio, Miller Edward, Maurer Mathew, Helmke Stephen, Fine Denise, Kurian Damian, Raiszadeh Farbod, Connors Lawreen, Prokaeva Tatiana, Pandey Shivda
Danon Disease Phase 1 RP-A501 Results: The First Single-Dose Intravenous Gene Therapy with Recombinant Adeno-Associated Virus (AAV9:LAMP2B) for a Monogenic CardiomyopathyGreenberg Barry, Coggins Matthew, Schwartz Jonathan, Rossano Joseph, Taylor Matthew, Colan Steven, Adler Eric, Ricks David, Yarabe Paul, Battiprolu Pavan, Shah Guarav, Patel Kinnari