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American Heart Association

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Final ID:

Discussant: Danon Disease Phase 1 RP-A501

  • Gillmore, Julian  ( UCL Centre for Amyloidosis , London , United Kingdom )
  • Taylor, Matthew  ( University of Colorado Health Sciences Center , Aurora , Colorado , United States )
  • Adler, Eric  ( Ucsd , La Jolla , California , United States )
  • Author Disclosures:
    Julian Gillmore: DO have relevant financial relationships ; Consultant:Alnylam, ATTRalus, AstraZeneca, Bridgebio, Lycia, Intellia, Pfizer:Active (exists now) | Matthew Taylor: DO NOT have relevant financial relationships | Eric Adler: DO have relevant financial relationships ; Employee:Lexeo Therapeutics:Active (exists now) ; Consultant:Kiniska Pharmaceuticals:Past (completed) ; Consultant:Abbott:Past (completed) ; Consultant:Abiomed:Past (completed) ; Ownership Interest:Papillion Therapeutics:Active (exists now) ; Other (please indicate in the box next to the company name):Solid Biosciences:Past (completed) ; Research Funding (PI or named investigator):Rocket Pharmaceuticals:Past (completed) ; Royalties/Patent Beneficiary:Rocket Pharmaceuticals:Active (exists now) ; Individual Stocks/Stock Options:Lexeo Therapeutics:Active (exists now) ; Royalties/Patent Beneficiary:Lexeo Therapeutics:Active (exists now)
Meeting Info:

Scientific Sessions 2024

2024

Chicago, Illinois

More abstracts on this topic:
ATTR-Specific Medication in Dual Pathology Aortic Stenosis and Transthyretin Cardiac Amyloidosis.

Nitsche Christian, Muller Steven, Gama Francisco, Hamdan Ashraf, Kelion Andrew, Schuster Andreas, Glaveckaite Sigita, Porcari Aldostefano, Autherith Maximilian, Hauptmann Laurenz, Halavina Kseniya, Dobner Stephan, Scully Paul, Moon James, Mascherbauer Julia, Biagini Elena, Stortecky Stefan, Maurer Matthew, Treibel Thomas, Rosenblum Hannah, Patel Kush, Longhi Simone, Yilmaz Ali, Merlo Marco, Papathanasiou Maria, Griffin Jan

Danon Disease Phase 1 RP-A501 Results: The First Single-Dose Intravenous Gene Therapy with Recombinant Adeno-Associated Virus (AAV9:LAMP2B) for a Monogenic Cardiomyopathy

Greenberg Barry, Coggins Matthew, Schwartz Jonathan, Rossano Joseph, Taylor Matthew, Colan Steven, Adler Eric, Ricks David, Yarabe Paul, Battiprolu Pavan, Shah Guarav, Patel Kinnari

More abstracts from these authors:
Danon Disease Phase 1 RP-A501 Results: The First Single-Dose Intravenous Gene Therapy with Recombinant Adeno-Associated Virus (AAV9:LAMP2B) for a Monogenic Cardiomyopathy

Greenberg Barry, Coggins Matthew, Schwartz Jonathan, Rossano Joseph, Taylor Matthew, Colan Steven, Adler Eric, Ricks David, Yarabe Paul, Battiprolu Pavan, Shah Guarav, Patel Kinnari

ATTR Genetic Screening and Subsequent Management in Underrepresented Populations-Bridging the Gap 10 minutes

Ruberg Frederick, Gillmore Julian

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