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American Heart Association

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Final ID:

Commentary: Gene Therapy for Cardiac Amyloid

  • Grogan, Martha  ( Mayo Clinic , Rochester , Minnesota , United States )
  • Grodin, Justin  ( UT SOUTHWESTERN , Dallas , Texas , United States )
  • Ambardekar, Amrut  ( University of Colorado , Aurora , Colorado , United States )
  • Author Disclosures:
    Martha Grogan: DO have relevant financial relationships ; Research Funding (PI or named investigator):BridgeBio:Active (exists now) ; Consultant:AstraZeneca:Active (exists now) ; Research Funding (PI or named investigator):Intellia:Active (exists now) ; Research Funding (PI or named investigator):NovoNordisk:Active (exists now) ; Consultant:NovoNordisk:Active (exists now) ; Consultant:Janssen:Active (exists now) ; Research Funding (PI or named investigator):Alnylam:Active (exists now) ; Research Funding (PI or named investigator):AstraZeneca:Active (exists now) | Justin Grodin: DO have relevant financial relationships ; Researcher:Pfizer:Active (exists now) ; Consultant:Tenax Therapeutics:Active (exists now) ; Consultant:Lumanity:Past (completed) ; Consultant:Ultromics:Past (completed) ; Advisor:AstraZeneca:Active (exists now) ; Advisor:Eidos / BridgeBIo:Active (exists now) ; Advisor:Alexion:Past (completed) ; Advisor:Novo Nordisk:Active (exists now) ; Research Funding (PI or named investigator):Eidos / BridgeBio:Past (completed) | Amrut Ambardekar: DO NOT have relevant financial relationships
Meeting Info:

Scientific Sessions 2025

2025

New Orleans, Louisiana

Session Info:

Rewriting the Code for Cardiac Amyloid: Novel Identification, Treatment, and Cure

Monday, 11/10/2025 , 01:30PM - 02:45PM

Featured Science

More abstracts on this topic:
Updated Phase 1 Clinical Trial Outcomes of CRISPR Gene Editing With Nexiguran Ziclumeran In Patients With Transthyretin Amyloidosis With Cardiomyopathy

Gillmore Julian, Smith Derek, Haagensen Alexandra, Olbertz Joy, Zhu Peijuan, Boiselle Carri, Leung Adia, Gutstein David, Sonderfan Alison, Walsh Liron, Fontana Marianna, Solomon Scott, Taubel Jorg, Gane Edward, Pilebro Bjorn, Adams David, Claggett Brian, Kachadourian Jessica, Rocha Ricardo

Primary results from the phase 2 randomized, placebo controlled, blinded trial of the monoclonal antibody coramitug in transthyretin amyloid cardiomyopathy (ATTR-CM)

Fontana Marianna, Kar Soumitra, Revanna Manjunatha, Sarswat Nitasha, Tsujita Kenichi, Maurer Mathew, Garcia-pavia Pablo, Grogan Martha, Shah Sanjiv, Engelmann Mads, Hovingh G. Kees, Kristen Arnt, Lim-watson Michelle, Malling Brian

More abstracts from these authors:
The Final Battle: Advanced Heart Failure and AF - HF Top 5 Take Aways

Ambardekar Amrut, Kittleson Michelle

Discussant: OLE & HELIOS-B

Grogan Martha, Kittleson Michelle, Nair Ajith, Grodin Justin, Ambardekar Amrut

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