Final ID: 27
Goyal Aman, Tariq Muhammad Daoud, Zahra Rubab, Jain Hritvik, Khan Rozi, Mahalwar Gauranga
A Phase I, Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Single Ascending Doses of N-acetylgalactosamine Small Interfering RNA Conjugate, BPR-30221616, in Healthy Participants, for Potential Treatment of Transthyretin AmyloidosisHan Xiaohong, Chen Rui, Cheng Xiwen, Zhang Langxi, Huang Haoxi, Fan Shengjun