Final ID:
Packer Milton
Nexiguran ziclumeran (nex-z, also known as NTLA-2001), an investigational in vivo CRISPR-based therapy for patients with transthyretin amyloidosis with cardiomyopathy (ATTR-CM): interim report of the Phase 1 studyFontana Marianna, Olbertz Joy, Zhu Peijuan, Boiselle Carri, Smith Derek, Leung Adia, Gutstein David, Sonderfan Alison, Walsh Liron, Gillmore Julian, Taubel Jorg, Gane Edward, Pilebro Bjorn, Adams David, Solomon Scott, Claggett Brian, Kachadourian Jessica, Rocha Ricardo