Final ID: Sa3133
Khanal Saugat, Yan Jiajie, Cao Yuanyuan, Ricchiuti Nikola, Nani Alma, Chen Wayne, Fill Michael, Bare Dan, Ai Xun
A Phase I, Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Single Ascending Doses of N-acetylgalactosamine Small Interfering RNA Conjugate, BPR-30221616, in Healthy Participants, for Potential Treatment of Transthyretin AmyloidosisHan Xiaohong, Chen Rui, Cheng Xiwen, Zhang Langxi, Huang Haoxi, Fan Shengjun